Prognia
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🇪🇺EU · EMAAuthorisedATC: N07XX18Orphan Medicine

Amvuttra(vutrisiran sodium)

Amyloid Neuropathies, Familial

Marketing Authorisation Holder: Alnylam Netherlands B.V.

EMA Authorisation: 15/09/2022

INN: vutrisiran

Indication

Treatment of hereditary transthyretin-mediated amyloidosis (hATTR amyloidosis) in adult patients with stage 1 or stage 2 polyneuropathy.

Official EMA Resources

View on EMA (ema.europa.eu)

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Medical disclaimer: This information is intended for qualified healthcare professionals. Always verify with the official EMA Summary of Product Characteristics (SmPC) before clinical use.