Prognia
Drug Database
🇪🇺EU · EMAAuthorisedATC: A16AB05

Aldurazyme(laronidase)

Mucopolysaccharidosis I

Marketing Authorisation Holder: Sanofi B.V.

EMA Authorisation: 09/06/2003

INN: laronidase

Indication

Aldurazyme is indicated for long-term enzyme replacement therapy in patients with a confirmed diagnosis of mucopolysaccharidosis I (MPS I; alpha-L-iduronidase deficiency) to treat the nonneurological manifestations of the disease.

Official EMA Resources

View on EMA (ema.europa.eu)

AI Drug & Interaction Analysis

Free account required

Ask Prognia AI about Aldurazyme — dosing recommendations, drug interactions, and current guideline evidence from ESC, EMA, NICE and more.

Medical disclaimer: This information is intended for qualified healthcare professionals. Always verify with the official EMA Summary of Product Characteristics (SmPC) before clinical use.